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Milestone 6.D

Initiate drug discovery efforts to develop novel therapeutic agents against at least 6 novel therapeutic targets (a minimum of three targets for presymptomatic and early stage disease and a minimum of three for advanced disease).

Success Criteria

  • Complete preclinical development, through IND filing, of at least 12 therapeutics agents against at least 3 novel targets (at least one novel target should be for presymptomatic disease).

  • Invest in the expansion of therapeutic modalities including natural products, gene therapy, antisense oligonucleotides, cell therapy, etc.

Research Implementation Area
Drug Development - Novel Targets
In Progress

Accomplishments/Implementation Activities

Funding Initiatives

Research Programs and Resources

Research Highlights

Relevant Recommendations